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sebelipase alfa (Kanuma®)

 

Status: Excluded due to NICE appraisal

Product meets AWMSG exclusion criteria due to NICE appraisal HST30: Sebelipase alfa for treating Wolman disease

Medicine details

Medicine name sebelipase alfa (Kanuma®)
Formulation 2 mg/ml concentrate for solution for infusion
Reference number 1305
Indication

For long-term enzyme replacement therapy in patients of all ages with lysosomal acid lipase deficiency

Company Alexion Pharma UK Ltd
BNF chapter Nutrition & blood
Assessment type N/A
Status Excluded due to NICE appraisal
Date of issue 17/12/2021
NICE guidance

HST30: Sebelipase alfa for treating Wolman disease

Further information

Initial FED ID737 for lysosomal acid lipase deficiency was not recommended. NICE appraising for Wolman disease population as ID3995 (14/12/2021)

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