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pegunigalsidase alfa (Elfabrio®)

 

Status: Excluded due to NICE appraisal

Product meets AWMSG exclusion criteria due to NICE appraisal TA915: Pegunigalsidase alfa for treating Fabry disease

Medicine details

Medicine name pegunigalsidase alfa (Elfabrio®)
Formulation intravenous infusion
Reference number 3683
Indication

Long-term enzyme replacement therapy in adult patients with confirmed diagnosis of Fabry disease (deficiency of alpha galactosidase).

Company Chiesi Limited
BNF chapter Nutrition & blood
Assessment type N/A
Status Excluded due to NICE appraisal
Date of issue 08/08/2023
NICE guidance

TA915: Pegunigalsidase alfa for treating Fabry disease

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