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cerliponase alfa (Brineura®)

 

Status: Excluded due to NICE appraisal

Product meets AWMSG exclusion criteria due to NICE appraisal HST12: Cerliponase alfa for treating neuronal ceroid lipofuscinosis type 2

Medicine details

Medicine name cerliponase alfa (Brineura®)
Formulation 150 mg solution for intracerebroventricular infusion
Reference number 2871
Indication

Treatment of neuronal ceroid lipofuscinosis type 2 (CLN2) disease, also known as tripeptidyl peptidase 1 (TPP1) deficiency

Company BioMarin International Ltd
BNF chapter Central nervous system
Submission type N/A
Status Excluded due to NICE appraisal
Date of issue 13/07/2017
NICE guidance

HST12: Cerliponase alfa for treating neuronal ceroid lipofuscinosis type 2

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